INFORMATION FOR FAMILIES

U.S. Expanded Access Policy

BridgeBio is on a mission to discover, create, test, and deliver transformative medicines to treat patients who suffer from genetic diseases, and is dedicated to serving these individuals, their families, and the communities they are part of through education, empathy, and awareness. [continue reading]

Canavan Disease

NTSAD Family Conference

A Closer Look at the Science

NTSAD Family Conference

NTSAD Family Conference

Aspa Webinar for Families

BBP-812 Gene Therapy Program for Canavan Disease

NTSAD - 46th Annual Family Conference

BBP-812 Gene Therapy Program for Canavan Disease

NTSAD - 45th Annual Family Conference

CANinform Natural History Study Design and COVID-19 Mitigation

The Joint 16th ICNA Congress & 49th Annual CNS Meeting

Natural History Study Design - Charlotte, NC

48th Annual Meeting of the Child Neurology Society

IV administration compared to IT and ICV - Barcelona, Spain

European Society for Gene & Cell Therapy

Natural History Study Design - Munich, Germany

Congress for Pediatrics and Adolescent Medicine, focused on pediatric neurology

Building a Natural History Study for Canavan Disease Washington, D.C.

EveryLife Foundation Annual Scientific Workshop

CANaspire Family Brochure

CANinform Family Brochure

Information and support are available for families affected by Canavan disease from advocacy organizations such as:

Families can also access resources on gene therapy, drug development and understanding clinical trials by visiting: